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Gene-editing in patient and humanized-mice primary muscle stem cells rescues dysferlin expression in dysferlin-deficient muscular dystrophy | 67 |
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Gene-editing in patient and humanized-mice primary muscle stem cells rescues dysferlin expression in dysferlin-deficient muscular dystrophy | 7 | 18 | 13 | 19 | 3 | 5 | 2 |
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41467_2024_Article_55086.pdf | 13 |