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Gene-editing in patient and humanized-mice primary muscle stem cells rescues dysferlin expression in dysferlin-deficient muscular dystrophy | 58 |
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Gene-editing in patient and humanized-mice primary muscle stem cells rescues dysferlin expression in dysferlin-deficient muscular dystrophy | 0 | 0 | 7 | 18 | 13 | 19 | 1 |
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41467_2024_Article_55086.pdf | 12 |