@article{Escobar2025,
author = {Escobar, Helena and Di Francescantonio, Silvia and Smirnova, Julia and Graf, Robin and Müthel, Stefanie and Marg, Andreas and Zhogov, Alexej and Krishna, Supriya and Metzler, Eric and Petkova, Mina and Daumke, Oliver and Kühn, Ralf and Spuler, Simone},
year = {2025},
language = {eng},
copyright = {https://creativecommons.org/licenses/by/4.0/},
title = {Gene-editing in patient and humanized-mice primary muscle stem cells rescues dysferlin expression in dysferlin-deficient muscular dystrophy},
volume = {16},
url = "http://dx.doi.org/10.17169/refubium-46117",
}
